Why rare diseases are an important medical and social issue
Lancet
.
2008 Jun 14;371(9629):2039-41.
doi: 10.1016/S0140-6736(08)60872-7.
Authors
Arrigo Schieppati
1
,
Jan-Inge Henter
,
Erica Daina
,
Anita Aperia
Affiliation
1
Clinical Research Centre for Rare Disease Aldo e Cele Daccò, Mario Negri Institute for Pharmacological Research, Bergamo, Italy. raredis@marionegri.it
PMID:
18555915
DOI:
10.1016/S0140-6736(08)60872-7
No abstract available
Publication types
Review
MeSH terms
Humans
Orphan Drug Production / legislation & jurisprudence*
Prevalence
Quality of Life
Rare Diseases / drug therapy
Rare Diseases / epidemiology*
Rare Diseases / genetics
Social Responsibility*
United States